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| ChEBI ID | CHEBI:71031 |
| ChEBI Name | orphan drug |
| Stars | |
| Definition | Any drug that has been developed specifically for treatment of a rare medical condition, the condition itself being known as an orphan disease. |
| Last Modified | 14 January 2016 |
| Submitter | Steve |
| Wikipedia |
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| ChEBI Ontology |
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| Outgoing Relation(s) |
| orphan drug (CHEBI:71031) is a drug (CHEBI:23888) |
| Incoming Relation(s) |
| 4-aminopyridine (CHEBI:34385) has role orphan drug (CHEBI:71031) |
| ACT-333679 (CHEBI:90848) has role orphan drug (CHEBI:71031) |
| carglumic acid (CHEBI:71028) has role orphan drug (CHEBI:71031) |
| isavuconazole (CHEBI:85979) has role orphan drug (CHEBI:71031) |
| isavuconazonium sulfate (CHEBI:85977) has role orphan drug (CHEBI:71031) |
| ivacaftor (CHEBI:66901) has role orphan drug (CHEBI:71031) |
| ixazomib (CHEBI:90942) has role orphan drug (CHEBI:71031) |
| ixazomib citrate (CHEBI:90939) has role orphan drug (CHEBI:71031) |
| lenvatinib (CHEBI:85994) has role orphan drug (CHEBI:71031) |
| lenvatinib mesylate (CHEBI:85995) has role orphan drug (CHEBI:71031) |
| lumacaftor (CHEBI:90951) has role orphan drug (CHEBI:71031) |
| macitentan (CHEBI:76607) has role orphan drug (CHEBI:71031) |
| Orkambi (CHEBI:90950) has role orphan drug (CHEBI:71031) |
| rifaximin (CHEBI:75246) has role orphan drug (CHEBI:71031) |
| selexipag (CHEBI:90844) has role orphan drug (CHEBI:71031) |
| sodium phenylbutyrate (CHEBI:75316) has role orphan drug (CHEBI:71031) |
| uridine triacetate (CHEBI:90914) has role orphan drug (CHEBI:71031) |
| Synonym | Source |
|---|---|
| orphan drugs | ChEBI |
| Manual Xrefs | Databases |
|---|---|
| Orphan_drug | Wikipedia |
| Citations |
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