EMD-35535
Human ornithine transcarbamylase expressed using mRNA lipid nanoparticles in human cells and PEGylated
EMD-35535
Single-particle4.3 Å
Deposition: 03/03/2023Map released: 16/08/2023
Last modified: 16/08/2023
Sample Organism:
Homo sapiens
Sample: Human ornithine transcarbamylase
Deposition Authors: Kondo K
,
Yamazaki K
,
Kubara K
,
Ishii S
,
Suzuki Y,
Miyazaki T,
Mitsuhashi K,
Ito M,
Tsukahara K
Sample: Human ornithine transcarbamylase
Deposition Authors: Kondo K
,
Yamazaki K
,
Kubara K
,
Ishii S
,
Suzuki Y,
Miyazaki T,
Mitsuhashi K,
Ito M,
Tsukahara K
Lipid nanoparticle-targeted mRNA formulation as a treatment for ornithine-transcarbamylase deficiency model mice.
Yamazaki K
,
Kubara K
,
Ishii S
,
Kondo K
,
Suzuki Y,
Miyazaki T,
Mitsuhashi K,
Ito M,
Tsukahara K
(2023) Mol Ther Nucleic Acids , 33 , 210 - 226
,
Kubara K
,
Ishii S
,
Kondo K
,
Suzuki Y,
Miyazaki T,
Mitsuhashi K,
Ito M,
Tsukahara K
(2023) Mol Ther Nucleic Acids , 33 , 210 - 226
Grant Support:
