Dbfetch
ID MP464889; SV 1; linear; other DNA; PAT; SYN; 7629 BP. XX AC MP464889; XX DT 15-MAY-2020 (Rel. 144, Created) DT 15-MAY-2020 (Rel. 144, Last updated, Version 1) XX DE Sequence 1 from Patent WO2020006458. XX KW . XX OS synthetic construct OC other sequences; artificial sequences. XX RN [1] RA SAHENK Z.; RT "RECOMBINANT ADENO-ASSOCIATED VIRUS PRODUCTS AND METHODS FOR TREATING LIMB RT GIRDLE MUSCULAR DYSTROPHY 2A"; RL Patent number WO2020006458-A1/1, 02-JAN-2020. RL RES INSTITUTE AT NATIONWIDE CHILDRENS HOSPITAL [US]. XX DR MD5; 3322ebf12309f6b4496145e87eb893b0. XX FH Key Location/Qualifiers FH FT source 1..7629 FT /organism="synthetic construct" FT /mol_type="other DNA" FT /note="Synthetic polynucleotide" FT /db_xref="taxon:32630" FT misc_feature 1..128 FT /note="AAV2 ITR" FT misc_feature 165..884 FT /note="tMCK promoter" FT misc_feature 937..1069 FT /note="chimeric intron" FT misc_feature 1101..1106 FT /note="Kozak Sequence" FT misc_feature 1107..3572 FT /note="CAPN3 polynucleotide" FT misc_feature 3581..3780 FT /note="poly A signal" FT misc_feature 3850..3977 FT /note="second AAV2 ITR" XX SQ Sequence 7629 BP; 1957 A; 1968 C; 2034 G; 1670 T; 0 other; gcgcgctcgc tcgctcactg aggccgcccg ggcaaagccc gggcgtcggg cgacctttgg 60 tcgcccggcc tcagtgagcg agcgagcgcg cagagaggga gtggccaact ccatcactag 120 gggttcctta atacgactca ctatagggcc gcaccggtaa gcttccacta cgggtctagg 180 ctgcccatgt aaggaggcaa ggcctgggga cacccgagat gcctggttat aattaacccc 240 aacacctgct gccccccccc ccccaacacc tgctgcctga gcctgagcgg ttaccccacc 300 ccggtgcctg ggtcttaggc tctgtacacc atggaggaga agctcgctct aaaaataacc 360 ctgtccctgg tggatccact acgggtctag gctgcccatg taaggaggca aggcctgggg 420 acacccgaga tgcctggtta taattaaccc caacacctgc tgcccccccc cccccaacac 480 ctgctgcctg agcctgagcg gttaccccac cccggtgcct gggtcttagg ctctgtacac 540 catggaggag aagctcgctc taaaaataac cctgtccctg gtggatccac tacgggtcta 600 ggctgcccat gtaaggaggc aaggcctggg gacacccgag atgcctggtt ataattaacc 660 ccaacacctg ctgccccccc ccccccaaca cctgctgcct gagcctgagc ggttacccca 720 ccccggtgcc tgggtcttag gctctgtaca ccatggagga gaagctcgct ctaaaaataa 780 ccctgtccct ggtggatcct ccctggggac agcccctcct ggctagtcac accctgtagg 840 ctcctctata taacccaggg gcacaggggc tgcccccggg tcacggtgga tatccctgca 900 ggtaccacgc gctgtaattg aactgggagt ggacacctgt ggagagaaag gcaaagtgga 960 tgtcagtaag accaataggt gcctatcaga aacgcaagag tcttctctgt ctcgacaagc 1020 ccagtttcta ttggtctcct taaacctgtc ttgtaacctt gatacttacg gagagcaact 1080 gcataagggc tagcctcgag gccaccatgc cgaccgtcat tagcgcatct gtggctccaa 1140 ggacagcggc tgagccccgg tccccagggc cagttcctca cccggcccag agcaaggcca 1200 ctgaggctgg gggtggaaac ccaagtggca tctattcagc catcatcagc cgcaattttc 1260 ctattatcgg agtgaaagag aagacattcg agcaacttca caagaaatgt ctagaaaaga 1320 aagttcttta tgtggaccct gagttcccac cggatgagac ctctctcttt tatagccaga 1380 agttccccat ccagttcgtc tggaagagac ctccggaaat ttgcgagaat ccccgattta 1440 tcattgatgg agccaacaga actgacatct gtcaaggaga gctaggggac tgctggtttc 1500 tcgcagccat tgcctgcctg accctgaacc agcaccttct tttccgagtc ataccccatg 1560 atcaaagttt catcgaaaac tacgcaggga tcttccactt ccagttctgg cgctatggag 1620 agtgggtgga cgtggttata gatgactgcc tgccaacgta caacaatcaa ctggttttca 1680 ccaagtccaa ccaccgcaat gagttctgga gtgctctgct ggagaaggct tatgctaagc 1740 tccatggttc ctacgaagct ctgaaaggtg ggaacaccac agaggccatg gaggacttca 1800 caggaggggt ggcagagttt tttgagatca gggatgctcc tagtgacatg tacaagatca 1860 tgaagaaagc catcgagaga ggctccctca tgggctgctc cattgatgat ggcacgaaca 1920 tgacctatgg aacctctcct tctggtctga acatggggga gttgattgca cggatggtaa 1980 ggaatatgga taactcactg ctccaggact cagacctcga ccccagaggc tcagatgaaa 2040 gaccgacccg gacaatcatt ccggttcagt atgagacaag aatggcctgc gggctggtca 2100 gaggtcacgc ctactctgtc acggggctgg atgaggtccc gttcaaaggt gagaaagtga 2160 agctggtgcg gctgcggaat ccgtggggcc aggtggagtg gaacggttct tggagtgata 2220 gatggaagga ctggagcttt gtggacaaag atgagaaggc ccgtctgcag caccaggtca 2280 ctgaggatgg agagttctgg atgtcctatg aggatttcat ctaccatttc acaaagttgg 2340 agatctgcaa cctcacggcc gatgctctgc agtctgacaa gcttcagacc tggacagtgt 2400 ctgtgaacga gggccgctgg gtacggggtt gctctgccgg aggctgccgc aacttcccag 2460 atactttctg gaccaaccct cagtaccgtc tgaagctcct ggaggaggac gatgaccctg 2520 atgactcgga ggtgatttgc agcttcctgg tggccctgat gcagaagaac cggcggaagg 2580 accggaagct aggggccagt ctcttcacca ttggcttcgc catctacgag gttcccaaag 2640 agatgcacgg gaacaagcag cacctgcaga aggacttctt cctgtacaac gcctccaagg 2700 ccaggagcaa aacctacatc aacatgcggg aggtgtccca gcgcttccgc ctgcctccca 2760 gcgagtacgt catcgtgccc tccacctacg agccccacca ggagggggaa ttcatcctcc 2820 gggtcttctc tgaaaagagg aacctctctg aggaagttga aaataccatc tccgtggatc 2880 ggccagtgaa aaagaaaaaa accaagccca tcatcttcgt ttcggacaga gcaaacagca 2940 acaaggagct gggtgtggac caggagtcag aggagggcaa aggcaaaaca agccctgata 3000 agcaaaagca gtccccacag ccacagcctg gcagctctga tcaggaaagt gaggaacagc 3060 aacaattccg gaacattttc aagcagatag caggagatga catggagatc tgtgcagatg 3120 agctcaagaa ggtccttaac acagtcgtga acaaacacaa ggacctgaag acacacgggt 3180 tcacactgga gtcctgccgt agcatgattg cgctcatgga tacagatggc tctggaaagc 3240 tcaacctgca ggagttccac cacctctgga acaagattaa ggcctggcag aaaattttca 3300 aacactatga cacagaccag tccggcacca tcaacagcta cgagatgcga aatgcagtca 3360 acgacgcagg attccacctc aacaaccagc tctatgacat cattaccatg cggtacgcag 3420 acaaacacat gaacatcgac tttgacagtt tcatctgctg cttcgttagg ctggagggca 3480 tgttcagagc ttttcatgca tttgacaagg atggagatgg tatcatcaag ctcaacgttc 3540 tggagtggct gcagctcacc atgtatgcct gagcggccgc ggggatccag acatgataag 3600 atacattgat gagtttggac aaaccacaac tagaatgcag tgaaaaaaat gctttatttg 3660 taaaatttgt gatgctattg ctttatttgt aaccattata agctgcaata aacaagttaa 3720 caacaacaat tgcattcatt ttatgtttca ggttcagggg gaggtgtggg aggttttttc 3780 ggatcctcta gagtcgacca gagcatggct acgtagataa gtagcatggc gggttaatca 3840 ttaactacaa ggaaccccta gtgatggagt tggccactcc ctctctgcgc gctcgctcgc 3900 tcactgaggc cgggcgacca aaggtcgccc gacgcccggg ctttgcccgg gcggcctcag 3960 tgagcgagcg agcgcgcagc tgcattaatg aatcggccaa cgcgcgggga gaggcggttt 4020 gcgtattggg cgctcttccg cttcctcgct cactgactcg ctgcgctcgg tcgttcggct 4080 gcggcgagcg gtatcagctc actcaaaggc ggtaatacgg ttatccacag aatcagggga 4140 taacgcagga aagaacatgt gagcaaaagg ccagcaaaag gccaggaacc gtaaaaaggc 4200 cgcgttgctg gcgtttttcc ataggctccg cccccctgac gagcatcaca aaaatcgacg 4260 ctcaagtcag aggtggcgaa acccgacagg actataaaga taccaggcgt ttccccctgg 4320 aagctccctc gtgcgctctc ctgttccgac cctgccgctt accggatacc tgtccgcctt 4380 tctcccttcg ggaagcgtgg cgctttctca tagctcacgc tgtaggtatc tcagttcggt 4440 gtaggtcgtt cgctccaagc tgggctgtgt gcacgaaccc cccgttcagc ccgaccgctg 4500 cgccttatcc ggtaactatc gtcttgagtc caacccggta agacacgact tatcgccact 4560 ggcagcagcc actggtaaca ggattagcag agcgaggtat gtaggcggtg ctacagagtt 4620 cttgaagtgg tggcctaact acggctacac tagaaggaca gtatttggta tctgcgctct 4680 gctgaagcca gttaccttcg gaaaaagagt tggtagctct tgatccggca aacaaaccac 4740 cgctggtagc ggtggttttt ttgtttgcaa gcagcagatt acgcgcagaa aaaaaggatc 4800 tcaagaagat cctttgatct tttctacggg gtctgacgct cagtggaacg aaaactcacg 4860 ttaagggatt ttggtcatga gattatcaaa aaggatcttc acctagatcc ttttaaatta 4920 aaaatgaagt tttaaatcaa tctaaagtat atatgagtaa aaatattccg gaattgccag 4980 ctggggcgcc ctctggtaag gttgggaagc cctgcaaagt aaactggatg gctttcttgc 5040 cgccaaggat ctgatggcgc aggggatcaa gatctgatca agagacagga tgaggatcgt 5100 ttcgcatgat tgaacaagat ggattgcacg caggttctcc ggccgcttgg gtggagaggc 5160 tattcggcta tgactgggca caacagacaa tcggctgctc tgatgccgcc gtgttccggc 5220 tgtcagcgca ggggcgcccg gttctttttg tcaagaccga cctgtccggt gccctgaatg 5280 aactgcagga cgaggcagcg cggctatcgt ggctggccac gacgggcgtt ccttgcgcag 5340 ctgtgctcga cgttgtcact gaagcgggaa gggactggct gctattgggc gaagtgccgg 5400 ggcaggatct cctgtcatcc caccttgctc ctgccgagaa agtatccatc atggctgatg 5460 caatgcggcg gctgcatacg cttgatccgg ctacctgccc attcgaccac caagcgaaac 5520 atcgcatcga gcgagcacgt actcggatgg aagccggtct tgtcgatcag gatgatctgg 5580 acgaagagca tcaggggctc gcgccagccg aactgttcgc caggctcaag gcgcgcatgc 5640 ccgacggcga ggatctcgtc gtgacccatg gcgatgcctg cttgccgaat atcatggtgg 5700 aaaatggccg cttttctgga ttcatcgact gtggccggct gggtgtggcg gaccgctatc 5760 aggacatagc gttggctacc cgtgatattg ctgaagagct tggcggcgaa tgggctgacc 5820 gcttcctcgt gctttacggt atcgccgctc ccgattcgca gcgcatcgcc ttctatcgcc 5880 ttcttgacga gttcttctga accggtaata ttattgaagc atttatcagg gttattgtct 5940 catgagcgga tacatatttg aatgtattta gaaaaataaa caaatagggg ttccgcgcac 6000 atttccccga aaagtgccac ctgacgtcta agaaaccatt attatcatga cattaaccta 6060 taaaaatagg cgtatcacga ggccctttcg tctcgcgcgt ttcggtgatg acggtgaaaa 6120 cctctgacac atgcagctcc cggagacggt cacagcttgt ctgtaagcgg atgccgggag 6180 cagacaagcc cgtcagggcg cgtcagcggg tgttggcggg tgtcggggct ggcttaacta 6240 tgcggcatca gagcagattg tactgagagt gcaccatatg cggtgtgaaa taccgcacag 6300 atgcgtaagg agaaaatacc gcatcaggaa cttccaacat ccaataaatc atacaggcaa 6360 ggcaaagaat tagcaaaatt aagcaataaa gcctcagagc ataaagctaa atcggttgta 6420 ccaaaaacat tatgaccctg taatactttt gcgggagaag cctttatttc aacgcaagga 6480 taaaaatttt tagaaccctc atatatttta aatgcaatgc ctgagtaatg tgtaggtaaa 6540 gattcaaacg ggtgagaaag gccggagaca gtcaaatcac catcaatatg atattcaacc 6600 gttctagctg ataaattcat gccggagagg gtagctattt ttgagaggtc tctacaaagg 6660 ctatcaggtc attgcctgag agtctggagc aaacaagaga atcgatgaac ggtaatcgta 6720 aaactagcat gtcaatcata tgtaccccgg ttgataatca gaaaagcccc aaaaacagga 6780 agattgtata agcaaatatt taaattgtaa acgttaatat tttgttaaaa ttcgcgttaa 6840 atttttgtta aatcagctca ttttttaacc aataggccga aatcggcaaa atcccttata 6900 aatcaaaaga atagaccgag atagggttga gtgttgttcc agtttggaac aagagtccac 6960 tattaaagaa cgtggactcc aacgtcaaag ggcgaaaaac cgtctatcag ggcgatggcc 7020 cactacgtga accatcaccc taatcaagtt ttttggggtc gaggtgccgt aaatcactaa 7080 atcggaaccc taaagggagc ccccgattta gagcttgacg gggaaagccg gcgaacgtgg 7140 cgagaaagga agggaagaaa gcgaaaggag cgggcgctag ggcgctggca agtgtagcgg 7200 tcacgctgcg cgtaaccacc acacccgccg cgcttaatgc gccgctacag ggcgcgtact 7260 atggttgctt tgacgagcac gtataacgtg ctttcctcgt tagaatcaga gcgggagcta 7320 aacaggaggc cgattaaagg gattttagac aggaacggta cgccagaatc ctgagaagtg 7380 tttttataat cagtgaggcc accgagtaaa agagtctgtc catcacgcaa attaaccgtt 7440 gtcgcaatac ttctttgatt agtaataaca tcacttgcct gagtagaaga actcaaacta 7500 tcggccttgc tggtaatatc cagaacaata ttaccgccag ccattgcaac ggaatcgcca 7560 ttcgccattc aggctgcgca actgttggga agggcgatcg gtgcgggcct cttcgctatt 7620 acgccagct 7629 //